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Acoramidis erhält positive CHMP-Empfehlung zur Behandlung von Transthyretin-Amyloidose mit Kardiomyopathie

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Der Ausschuss für Humanarzneimittel (Committee for Medicinal Products for Human Use, CHMP) der Europäischen Arzneimittel-Agentur hat die Zulassung für Acoramidis auf Basis der positiven Ergebnisse der Phase-III-Studie ATTRibute-CM1 empfohlen / Die endgültige Entscheidung der Europäischen Kommission wird in den nächsten Monaten erwartet / Acoramidis ist ein oral einzunehmender, nahezu vollständiger (≥90 %) Stabilisator von Transthyretin (TTR)2 zur Behandlung erwachsener Patienten mit Transthyretin-Amyloidose mit Kardiomyopathie (ATTR-CM)

Der Ausschuss für Humanarzneimittel (CHMP) der Europäischen Arzneimittel-Agentur (EMA) hat Acoramidis, ein selektiver niedermolekularer oral verabreichter Stabilisator von Transthyretin (TTR), zur Marktzulassung in der Europäischen Union empfohlen. Der Wirkstoff ist zur Behandlung erwachsener Patienten mit
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